
Biotech in gene therapies for neurodegenerative disease

Who they are & what they do
Company overview chevron_right
Developing a novel gene therapy for Huntington's disease, one of the largest unmet needs among rare neurodegenerative disorders. Its core technology is a "molecular switch" based on the MTF1 gene, designed to reduce the toxicity of the mutant huntingtin protein that drives disease progression, delivered via AAV or mRNA vectors.
The company was founded in April 2024 by a team of University of Padua scientists, with support from the Golinelli Foundation and Italy's PNRR biotech funding stream, and is completing its formal recognition as a University of Padua academic spin-off — a step needed to access private and venture capital to scale its R&D program.
Key clients & traction
ItalypublicWebsite: lock Confidential
Why look at this deal
Highlights
- 01Targets Huntington's disease
- 02Proprietary MTF1 switch
- 03University of Padua
- 04Golinelli Foundation backing
- 05PNRR-funded research
Deal snapshot
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